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Lysosomal and network alterations in human mucopolysaccharidosis type VII iPSC-derived neurons.

Bayó-Puxan N, Terrasso AP, Creyssels S, Simão D, Begon-Pescia C, Lavigne M, Salinas S, Bernex F, Bosch A, Kalatzis V, Levade T, Cuervo AM, Lory P, Consiglio A, Brito C, Kremer E.

Sci Rep

2018 Nov 9 / vol 8(1) / pages 16644

Lire sur PubMed

10.1038/s41598-018-34523-3

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